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    • Novel Genome-Editing Tools to Model and Correct Primary Immunodeficiencies 

      Ott de Bruin, Lisa M.; Volpi, Stefano; Musunuru, Kiran (Frontiers Media S.A., 2015)
      Severe combined immunodeficiency (SCID) and other severe non-SCID primary immunodeficiencies (non-SCID PID) can be treated by allogeneic hematopoietic stem cell (HSC) transplantation, but when histocompatibility leukocyte ...