Browsing Faculty of Arts and Sciences by Keyword "ZFN"
Now showing items 1-2 of 2
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Improving Zinc Finger Nucleases - Strategies for Increasing Gene Editing Activities and Evaluating Off-Target Effects
(2012-08-23)Zinc finger nucleases (ZFNs) induce double-strand DNA breaks at specific recognition sites. ZFNs can dramatically increase the efficiency of incorporating desired insertions, deletions, or substitutions in living cells. ... -
Novel Genome-Editing Tools to Model and Correct Primary Immunodeficiencies
(Frontiers Media S.A., 2015)Severe combined immunodeficiency (SCID) and other severe non-SCID primary immunodeficiencies (non-SCID PID) can be treated by allogeneic hematopoietic stem cell (HSC) transplantation, but when histocompatibility leukocyte ...