Newby, GregoryYen, Jonathan S.Woodard, Kaitly J.Mayuranathan, ThiyagarajLazzarotto, Cicera R.Li, YichaoSheppard-Tillman, HeatherPorter, Shaina N.Yao, YuMayberry, KalinEverette, Kelcee A.Jang, YoonjeongPodracky, Christopher J.Thaman, ElizabethLechauve, ChristopheSharma, AkshayHenderson, Jordana M.Richter, MichelleZhao, KevinMiller, ShannonWang, TinaKoblan, LukeMcCaffrey, Anton P.Tisdale, John F.Kalfa, TheodosiaPruett-Miller, Shondra M.Tsai, ShengdarWeiss, Mitchell J.Liu, David2022-02-172021-06-02Newby, Gregory, Jonathan S. Yen, Kaitly J. Woodard, Thiyagaraj Mayuranathan, Cicera R. Lazzarotto, Yichao Li, Heather Sheppard-Tillman et al. "Base editing of haematopoietic stem cells rescues sickle cell disease in mice." Nature (London) 595, no. 7866 (2021): 295-302. DOI: 10.1038/s41586-021-03609-w0028-08361476-4687https://nrs.harvard.edu/URN-3:HUL.INSTREPOS:37370844en-USMultidisciplinaryBase editing of haematopoietic stem cells rescues sickle cell disease in miceJournal Article2022-02-1710.1038/s41586-021-03609-w